Gene therapy cures “bubble babies”

bubble kids

There is new hope for the so-called "bubble children", those children affected by ADA-SCID, a very serious and rare form of hereditary immunodeficiency that makes them easy prey to viruses and bacteria. There is a new treatment method, obtained by modifying patients' stem cells through the insertion of the gene responsible for the disease, revised and corrected. An achievement, called gene therapy, which will allow these children to live in the real world, outside the bubble that protects them day and night. Luigi Naldini, director … Read more